CNBC is premiering a documentary special titled "CNBC Cures: Defying Rare Disease," focusing on families navigating rare genetic conditions.
The special highlights the extreme financial burden of emerging treatments, noting that saving a life with current gene therapies can cost around $1.2 million, with advocates hoping to eventually reduce that cost to $700,000.
Medical professionals and advocates emphasize that medicine is currently in a "golden age" of exploding science and technology, moving past the theoretical cusp into active, life-saving gene therapies.